Enterprise Value

3.138B

Cash

213.4M

Avg Qtr Burn

-49.05M

Short % of Float

7.46%

Insider Ownership

4.49%

Institutional Own.

66.87%

Qtr Updated

12/31/23


Drug Pipeline

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Drug & IndicationStage & EventCatalyst Date
Plozasiran (ARO-APOC3) Details
Familial chylomicronemia syndrome

Big Mover™

Susp. Mover™

Phase 3

Data readout

Fazirsiran (ARO-AAT) (TAK-999) Details
Severe alpha-1 antitrypsin deficiency, Liver disease

Phase 3

Update

Plozasiran (ARO-APOC3) Details
Severe hypertriglyceridemia

Phase 3

Initiation

Phase 2b

Update

Phase 2b

Update

ARO-ANG3 Details
Dyslipidemia

Phase 2

Update

ARO-DM1 Details
Myotonic Dystrophy Type 1

Phase 1/2

Data readout

ARO-CFB Details
Complement mediated diseases, Kidney disease, IgA nephropathy

Phase 1/2

Data readout

ARO-C3 (RNAi) Details
Renal disease, Paroxysmal nocturnal hemoglobinuria

Phase 1/2

Data readout

ARO-MMP7 Details
Idiopathic pulmonary fibrosis

Phase 1/2

Data readout

ARO-MUC5AC Details
Lung disease, Muco-Obstructive Lung Diseases

Phase 1/2

Data readout

ARO-RAGE Details
Muco-Obstructive Lung Diseases, Inflammatory disease, Asthma

Phase 1/2

Data readout

ARO-DUX4 Details
Facioscapulohumeral muscular dystrophy

Phase 1/2

Initiation

Failed

Discontinued

ARO-HSD Details
Liver disease, Non-alcoholic steatohepatitis

Failed

Discontinued