Enterprise Value

1.774B

Cash

410.7M

Avg Qtr Burn

-30.65M

Short % of Float

26.02%

Insider Ownership

1.24%

Institutional Own.

93.70%

Qtr Updated

06/30/23


Drug Pipeline

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Drug & IndicationStage & EventCatalyst Date

Approved

Quarterly sales

Orladeyo (Berotralstat) Details
Rare diseases, Rare genetic disease, Hereditary angioedema

Approved

Quarterly sales

BCX10013 (Oral Factor D inhibitor) Details
Complement mediated diseases, Paroxysmal nocturnal hemoglobinuria

Phase 1

Initiation

BCX9250 (ALK2 inhibitor) Details
Fibrodysplasia ossificans progressiva

Failed

Discontinued

Failed

Discontinued

BCX9930 (Oral Factor D inhibitor) Details
Paroxysmal nocturnal hemoglobinuria

Failed

Discontinued