Enterprise Value
5.41B
Cash
2.394B
Avg Qtr Burn
-114M
Short % of Float
6.42%
Insider Ownership
0.76%
Institutional Own.
95.01%
Qtr Updated
06/30/23
Drug Pipeline
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Drug & Indication | Stage & Event | Catalyst Date |
---|---|---|
QALSODY™ (Tofersen) Details Amyotrophic lateral sclerosis | Approved Update | |
SPINRAZA Details Spinal muscular atrophy | Approved Quarterly sales | |
PDUFA Approval decision | ||
IONIS-APOCIII-LRx (Olezarsen) Details Familial chylomicronemia syndrome | NDA Submission | |
ION363 Details ALS (Amyotrophic Lateral Sclerosis) | Phase 3 Data readout | |
Eplontersen (AKCEA-TTR-LRx) Details Diabetic cardiomyopathy, Transthyretin Amyloid Cardiomyopathy, Transthyretin amyloidosis | Phase 3 Data readout | |
IONIS-APOCIII-LRx (Olezarsen) Details Severe hypertriglyceridemia | Phase 3 Data readout | |
Donidalorsen (IONIS-PKK-LRx) Details Hereditary angioedema | Phase 3 Data readout | |
Bepirovirsen (IONIS-HBVRx) Details Hepatitis B | Phase 3 Update | |
IONIS-FB-LRx Details IgA nephropathy | Phase 3 Initiation | |
Zilganersen (ION373) Details Alexander Disease | Phase 2/3 Data readout | |
ION839 / AZD2693 Details Non-alcoholic steatohepatitis | Phase 2b Data readout | |
ION224 Details Non-alcoholic steatohepatitis | Phase 2b Data readout | |
Fesomersen (IONIS-FXI-LRx) Details Hepatitis B | Phase 2b Update | |
IONIS-MAPTRx (BIIB080) Details Alzheimer's disease | Phase 2 Data readout | |
IONIS-FB-LRx Details Geographic atrophy | Phase 2 Data readout | |
Tominersen (IONIS-HTT Rx) Details Huntington's disease | Phase 2 Update | |
IONIS-AGT-LRx Details Pulmonary hypertension, Heart failure | Phase 2 Update | |
IONIS-ENaC-2.5Rx (antisense medicine) Details Cystic fibrosis | Failed Discontinued | |
Cimdelirsen (IONIS-GHR-LRx) Details Acromegaly | Failed Discontinued |