MGTX - MeiraGTx

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MeiraGTx NasdaqGS:MGTX MeiraGTx Holdings plc, a clinical stage genetics medicines company, focusing on developing treatments for patients with serious diseases. The company develops various therapies for ocular diseases, including inherited retinal diseases and large degenerative ocular diseases; neurodegenerative diseases; and xerostomia. It is also developing AAV-AQP1 in Phase 2 trial for radiation-induced grade 2/3 radiation-induced xerostomia, as well as in Phase ½ trial for Sjogren's syndrome; AAV-GAD in Phase 2 trial for Parkinson's disease; AAV-RPE65 in Phase 2 trial for RPE65-associated retinal dystrophy; and AAV-CNGB3 and AAV-CNGA3, which are both in Phase 2 trial for achromatopsia, as well as offers AAV-AIPL1 for Leber congenital amaurosis (LCA) 4. In addition, the company's products under preclinical development include AAV-RDH12 for retinol dehydrogenase 12 mutation-associated retinal dystrophy; AAV-BBS10 for Bardet-Biedl syndrome (BBS) due to BBS10 mutations; AAV-RetGC for LCA type 1; and AAV-UPF1 for amyotrophic lateral sclerosis, as well as programs for Alzheimer's disease, and wet and dry neovascular age related macular degeneration. Further, it provides riboswitch platform for the delivery of metabolic peptides; and cell therapies for oncology, autoimmune disease, and long term intractable pain. The company has collaborations with Johnson & Johnson Innovative Medicine for the research, development, and commercialization of gene therapies for the treatment of inherited retinal disease; and Hologen Limited for the research, development, manufacture, and commercialization of AAV-GAD investigational gene therapy for the treatment of Parkinson's disease, AAV-BDNF investigational gene therapy for genetic obesity disorders, and other genetic medicines to the central nervous system. MeiraGTx Holdings plc was founded in 2015 and is based in New York, New York.

Location: 450 East 29th Street, New York, NY, 10016, United States | Website: https://meiragtx.com | Industry: Biotechnology | Sector: Healthcare


Market Cap

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52 Wk Range

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Previous Close

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Open

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Day Range

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Volume

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Avg Volume

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Enterprise Value

445.1M

Cash

66.52M

Avg Qtr Burn

-26.15M

Short % of Float

7.73%

Insider Ownership

24.18%

Institutional Own.

60.08%

Qtr Updated

03/31/25


Drug Pipeline

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Drug & IndicationStage & EventCatalyst Date
Bota-vec (Botaretigene sparoparvovec) (AAV-RPGR) Details
X-linked retinitis pigmentosa, Genetic disorder, Eye disease

Phase 3

Update

AAV-RPE65 Details
Eye disease , Retinal dystrophy

Phase 3

Initiation

AAV-CNGB3 Details
Achromatopsia, Genetic disorder, Autosomal recessive congenital ichthyosis , Skin disease/disorder

Phase 2b

Update

AAV-CNGA3 Details
Achromatopsia

Phase 2b

Update

AAV2-hAQP1 Details
Salivary gland

Phase 2

Data readout

AAV-GAD Details
Parkinson's disease

Phase 2

Update