MIRM - Mirum Pharmaceuticals

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Mirum Pharmaceuticals NASDAQ:MIRM Mirum Pharmaceuticals, Inc. is a clinical-stage biopharmaceutical company focused on the development and commercialization of a late-stage pipeline of novel therapies for debilitating liver diseases. Mirum's lead product candidate, maralixibat, is an investigational oral drug in development for Alagille syndrome (ALGS), progressive familial intrahepatic cholestasis (PFIC), and biliary atresia. Mirum has submitted an NDA for maralixibat in the treatment of cholestatic pruritus in patients with ALGS. Additionally, Mirum's marketing authorization application for the treatment of pediatric patients with PFIC2 has been accepted for review (validated) by the European Medicines Agency.

Location: | Website: mirumpharma.com | Industry: Research and Development in Biotechnology | Sector: Professional, Scientific, and Technical Services


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52 Wk Range

$ - $

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Volume

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Avg Volume

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Enterprise Value

1.931B

Cash

278.4M

Avg Qtr Burn

-5.858M

Short % of Float

19.89%

Insider Ownership

2.21%

Institutional Own.

-

Qtr Updated

06/30/24


Drug Pipeline

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Drug & IndicationStage & EventCatalyst Date
LIVMARLI (Maralixibat) Details
Chronic pruritus, Alagille syndrome

Approved

Quarterly sales

LIVMARLI (Maralixibat) Details
Liver disease, Progressive familial intrahepatic cholestasis

Approved

Quarterly sales

Chenodal® (chenodiol) Details
Cerebrotendinous xanthomatosis

NDA

Acceptance for review

LIVMARLI (Maralixibat) Details
Bile duct disease, Rare diseases

Phase 2b

Update

Volixibat (VANTAGE) Details
Primary biliary cholangitis, Liver disease

Phase 2b

Update

Volixibat (VISTAS) Details
Liver disease, Primary sclerosing cholangitis

Phase 2b

Update

Volixibat (OHANA) Details
Liver disease, Intrahepatic Cholestasis of Pregnancy

Failed

Discontinued