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Mirum Pharmaceuticals NASDAQ:MIRM Mirum Pharmaceuticals, Inc. is a clinical-stage biopharmaceutical company focused on the development and commercialization of a late-stage pipeline of novel therapies for debilitating liver diseases. Mirum's lead product candidate, maralixibat, is an investigational oral drug in development for Alagille syndrome (ALGS), progressive familial intrahepatic cholestasis (PFIC), and biliary atresia. Mirum has submitted an NDA for maralixibat in the treatment of cholestatic pruritus in patients with ALGS. Additionally, Mirum's marketing authorization application for the treatment of pediatric patients with PFIC2 has been accepted for review (validated) by the European Medicines Agency.
Location: | Website: mirumpharma.com | Industry: Research and Development in Biotechnology | Sector: Professional, Scientific, and Technical Services
Market Cap
NaN
52 Wk Range
$ - $
Previous Close
$N/A
Open
$N/A
Day Range
N/A - N/A
Volume
N/A
Avg Volume
N/A
Enterprise Value
1.954B
Cash
280.3M
Avg Qtr Burn
N/A
Short % of Float
16.93%
Insider Ownership
2.14%
Institutional Own.
-
Qtr Updated
12/31/24
Drug Pipeline
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Drug & Indication | Stage & Event | Catalyst Date |
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LIVMARLI (Maralixibat) Details Liver disease, Progressive familial intrahepatic cholestasis | Approved Quarterly sales | |
CTEXLI™ (chenodiol) Tablets Details Cerebrotendinous xanthomatosis | Approved Quarterly sales | |
LIVMARLI (Maralixibat) Details ALGS (Alagille syndrome), PFIC (Progressive Familial Intrahepatic Cholestasis) | Approved Quarterly sales | |
Volixibat Details Primary biliary cholangitis, Liver disease | Phase 2b Update | |
Volixibat Details Liver disease, Primary sclerosing cholangitis | Phase 2b Update | |
MRM-3379 Details Fragile X syndrome | Phase 2 Initiation | |
Volixibat Details Liver disease, Intrahepatic Cholestasis of Pregnancy | Failed Discontinued | |
LIVMARLI (Maralixibat) Details Rare diseases, Bile duct disease | Failed Discontinued |