Pharming Group N.V., a biopharmaceutical company, develops and commercializes protein replacement therapies and precision medicines for the treatment of rare diseases in the United States, Europe, and internationally. The company's lead product is RUCONEST, a recombinant C1 esterase inhibitor for the treatment of acute attacks in adult and adolescent patients with acute hereditary angioedema (HAE); and Joenja (leniolisib), an oral small molecule PI3K? inhibitor for the treatment of activated phosphoinositide 3-kinase delta syndrome. It also develops OTL-105, an investigational ex-vivo autologous hematopoietic stem cell gene therapy for the treatment of HAE. It has a development collaboration and license agreement with Novartis; and a strategic collaboration agreement with Orchard Therapeutics plc for research, development, manufacturing, and commercialization of OTL-105. Pharming Group N.V. was incorporated in 1988 and is headquartered in Leiden, the Netherlands. Show more
Darwinweg 24, Leiden, 2333 CR, Netherlands
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Market Cap
1.136B
52 Wk Range
$7.50 - $21.34
Previous Close
$16.37
Open
$16.47
Volume
10,217
Day Range
$16.29 - $16.58
Enterprise Value
1.11B
Cash
166.2M
Avg Qtr Burn
N/A
Insider Ownership
0.00%
Institutional Own.
0.21%
Qtr Updated
09/30/25
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| Drug & Indication | Stage & Event | Catalyst Date |
|---|---|---|
Joenja® (leniolisib) Details Activated Phosphoniositide 3-kinase Delta Syndrome | Approved Quarterly sales | |
Leniolisib Details Activated Phosphoniositide 3-kinase Delta Syndrome (APDS in children 4–11) (label expansion) | sNDA FDA meeting | |
KL1333 Details Mitochondrial disease, primary mitochondrial myopathies | Phase 3 Data readout | |
Leniolisib Details Immunodeficiency | Phase 2 Data readout |
