Enterprise Value

3.984B

Cash

890.9M

Avg Qtr Burn

-14.54M

Short % of Float

10.50%

Insider Ownership

2.37%

Institutional Own.

-

Qtr Updated

03/31/24


Drug Pipeline

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Drug & IndicationStage & EventCatalyst Date
Emflaza (deflazacort) Details
Duchenne muscular dystrophy

Approved

Quarterly sales

Evrysdi (riskiplam) Details
Spinal muscular atrophy

Approved

Quarterly sales

Upstaza (PTC-AADC) Details
Aromatic L-amino acid decarboxylase deficiency

PDUFA

Approval decision

Translarna (ataluren) Details
Duchenne muscular dystrophy

NDA

Resubmission

Vatiquinone (PTC743) Details
Friedreich’s Ataxia

NDA

Submission

NDA

Submission

PTC518 Details
Huntington's disease

Phase 2

Data readout

Utreloxastat Details
Amyotrophic lateral sclerosis

Phase 2

Data readout

Vatiquinone (PTC743) Details
Epilepsy, Mitochondrial disease

Failed

Discontinued

Failed

Discontinued