Enterprise Value
540.7M
Cash
338.7M
Avg Qtr Burn
-48.24M
Short % of Float
11.82%
Insider Ownership
7.32%
Institutional Own.
91.18%
Qtr Updated
03/31/24
Drug Pipeline
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Drug & Indication | Stage & Event | Catalyst Date |
---|---|---|
RGX-121 Details Mucopolysaccharidosis type II, Rare diseases, Pulmonary arterial hypertension, Lung disease, Rare genetic disease, Genetic disorder, Mucopolysaccharidoses | BLA Submission | |
ABBV-RGX-314 (Subretinal Delivery) Details Eye disease , Wet age-related macular degeneration , Age-related macular degeneration | Phase 2 Data readout | |
ABBV-RGX-314 (Suprachoroidal Delivery) Details Eye disease , Diabetic retinopathy , Diabetes | Phase 2 Data readout | |
ABBV-RGX-314 (Suprachoroidal Delivery) Details Eye disease , Wet age-related macular degeneration , Age-related macular degeneration | Phase 2 Data readout | |
RGX-202 Details Rare diseases, Genetic disorder, Rare genetic disease, Duchenne muscular dystrophy | Phase 1/2 Data readout | |
RGX-381 Details Central nervous system illness | Phase 1/2 Data readout | |
RGX-111 Details Mucopolysaccharidoses, Rare genetic disease, Genetic disorder, Rare diseases, Mucopolysaccharidosis Type 1 | Phase 1/2 Update | |
RGX-181 Details Central nervous system illness, Batten Disease | Phase 1 Data readout |