Enterprise Value

540.7M

Cash

338.7M

Avg Qtr Burn

-48.24M

Short % of Float

11.82%

Insider Ownership

7.32%

Institutional Own.

91.18%

Qtr Updated

03/31/24


Drug Pipeline

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Drug & IndicationStage & EventCatalyst Date
RGX-121 Details
Mucopolysaccharidosis type II, Rare diseases, Pulmonary arterial hypertension, Lung disease, Rare genetic disease, Genetic disorder, Mucopolysaccharidoses

BLA

Submission

ABBV-RGX-314 (Subretinal Delivery) Details
Eye disease , Wet age-related macular degeneration , Age-related macular degeneration

Phase 2

Data readout

ABBV-RGX-314 (Suprachoroidal Delivery) Details
Eye disease , Diabetic retinopathy , Diabetes

Phase 2

Data readout

ABBV-RGX-314 (Suprachoroidal Delivery) Details
Eye disease , Wet age-related macular degeneration , Age-related macular degeneration

Phase 2

Data readout

RGX-202 Details
Rare diseases, Genetic disorder, Rare genetic disease, Duchenne muscular dystrophy

Phase 1/2

Data readout

RGX-381 Details
Central nervous system illness

Phase 1/2

Data readout

RGX-111 Details
Mucopolysaccharidoses, Rare genetic disease, Genetic disorder, Rare diseases, Mucopolysaccharidosis Type 1

Phase 1/2

Update

RGX-181 Details
Central nervous system illness, Batten Disease

Phase 1

Data readout