Enterprise Value

115.8M

Cash

54.42M

Avg Qtr Burn

-51.8M

Short % of Float

7.45%

Insider Ownership

7.73%

Institutional Own.

50.81%

Qtr Updated

03/31/24


Drug Pipeline

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Drug & IndicationStage & EventCatalyst Date
Giroctocogene fitelparvovec (SB-525 / PF-07055480) Details
Blood disorder, Rare diseases, Hemophilia, Rare genetic disease

Phase 3

Update

TX-200 Details
Kidney disease, Kidney transplantation

Phase 1/2

Data readout

ST-920 (isaralgagene civaparvovec) Details
Fabry disease, Rare genetic disease

Phase 1/2

Update

BIVV003 (SAR445136) Details
Sickle cell disease, Blood disorder

Failed

Discontinued

ST-400 Details
Blood disorder, Beta thalessemia

Failed

Discontinued

SB-913 Details
Genetic disorder, Rare diseases, Mucopolysaccharidoses, Rare genetic disease, Mucopolysaccharidosis type II

Failed

Discontinued