Enterprise Value

4.494B

Cash

333.5M

Avg Qtr Burn

-137.5M

Short % of Float

18.57%

Insider Ownership

14.32%

Institutional Own.

94.47%

Qtr Updated

03/31/24


Drug Pipeline

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Drug & IndicationStage & EventCatalyst Date
SYFOVRE™(Intravitreal pegcetacoplan) Details
Age-related macular degeneration, Geographic atrophy

Approved

Quarterly sales

Empaveli (systemic pegcetacoplan) (APL-2) Details
Paroxysmal nocturnal hemoglobinuria

Approved

Quarterly sales

Systemic pegcetacoplan (APL-2) Details
C3 Glomerulopathy, Immune complex membranoproliferative glomerulonephritis

Phase 3

Data readout

Systemic pegcetacoplan (APL-2) Details
Hematopoietic stem cell transplantation thrombotic microangiopathies

Phase 2

Data readout

Systemic pegcetacoplan (APL-2) Details
Immune complex membranoproliferative glomerulonephritis, C3 Glomerulopathy

Phase 2

Update

APL-3007 (small interfering RNA silencing C3) Details
Autoimmune disease, Inflammatory disease

Phase 1

Data readout

Systemic pegcetacoplan (APL-2) Details
Amyotrophic lateral sclerosis

Failed

Discontinued

Intravenous APL-9 Details
ARDS (Acute respiratory distress syndrome), TMA (Thrombotic microangiopathies)

Failed

Discontinued

Failed

Discontinued