APLS - Apellis Pharmaceuticals

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Apellis Pharmaceuticals NASDAQ:APLS Apellis Pharmaceuticals, Inc. is a global biopharmaceutical company that is committed to leveraging courageous science, creativity, and compassion to deliver life-changing therapies. Leaders in targeted C3 therapies, the company aims to develop transformative therapies for a broad range of debilitating diseases that are driven by excessive activation of the complement cascade, including those within hematology, ophthalmology, nephrology, and neurology.

Location: 100 Fifth Avenue, Massachusetts, 02451, United States | Website: apellis.com | Industry: Pharmaceutical Preparation Manufacturing | Sector: Manufacturing


Market Cap

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52 Wk Range

$ - $

Previous Close

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Open

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Day Range

N/A - N/A

Volume

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Avg Volume

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Enterprise Value

3.467B

Cash

368M

Avg Qtr Burn

-102.1M

Short % of Float

18.64%

Insider Ownership

14.28%

Institutional Own.

96.96%

Qtr Updated

06/30/24


Drug Pipeline

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Drug & IndicationStage & EventCatalyst Date
SYFOVRE™(Intravitreal pegcetacoplan) Details
Age-related macular degeneration, Geographic atrophy

Approved

Quarterly sales

Empaveli (systemic pegcetacoplan) (APL-2) Details
Paroxysmal nocturnal hemoglobinuria

Approved

Quarterly sales

Systemic pegcetacoplan (APL-2) Details
Immune complex membranoproliferative glomerulonephritis, C3 Glomerulopathy

sNDA

Submission

Systemic pegcetacoplan (APL-2) Details
Hematopoietic stem cell transplantation thrombotic microangiopathies

Phase 2

Data readout

Systemic pegcetacoplan (APL-2) Details
Immune complex membranoproliferative glomerulonephritis, C3 Glomerulopathy

Phase 2

Update

APL-3007 (small interfering RNA silencing C3) Details
Autoimmune disease, Inflammatory disease

Phase 1

Data readout

Systemic pegcetacoplan (APL-2) Details
Amyotrophic lateral sclerosis

Failed

Discontinued

Intravenous APL-9 Details
ARDS (Acute respiratory distress syndrome), TMA (Thrombotic microangiopathies)

Failed

Discontinued

Failed

Discontinued